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Modeling and Rescue of RP2 Retinitis Pigmentosa Using iPSC-Derived Retinal Organoids.
Lane, Amelia ; Jovanovic, Katarina ; Shortall, Ciara ; Ottaviani, Daniele ; Panes, Anna Brugulat ; Schwarz, Nele ; Guarascio, Rosellina ; Hayes, Matthew J ; Palfi, Arpad ; Chadderton, Naomi ... show 3 more
Lane, Amelia
Jovanovic, Katarina
Shortall, Ciara
Ottaviani, Daniele
Panes, Anna Brugulat
Schwarz, Nele
Guarascio, Rosellina
Hayes, Matthew J
Palfi, Arpad
Chadderton, Naomi
Advisors
Editors
Other Contributors
Departments
Date
2020-06-11
Date Submitted
Keywords
AAV
CRISPR gene editing
cell death
disease modeling
Gene Therapy
genetic
inherited disease
retinal degeneration
retinal organoid
stem cell
CRISPR gene editing
cell death
disease modeling
Gene Therapy
genetic
inherited disease
retinal degeneration
retinal organoid
stem cell
Other Subjects
Subject Mesh
Planned Date
Start Date
Collaborators
Principal Investigators
Files
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mmc3.pdf
Adobe PDF, 5.13 MB
Alternative Titles
Publisher
Abstract
Language
en
Citation
ISSN
eISSN
2213-6711
ISBN
DOI
10.1016/j.stemcr.2020.05.007
PMID
32531192
