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Modeling and Rescue of RP2 Retinitis Pigmentosa Using iPSC-Derived Retinal Organoids.

Lane, Amelia
Jovanovic, Katarina
Shortall, Ciara
Ottaviani, Daniele
Panes, Anna Brugulat
Schwarz, Nele
Guarascio, Rosellina
Hayes, Matthew J
Palfi, Arpad
Chadderton, Naomi
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Date
2020-06-11
Date Submitted
Keywords
AAV
CRISPR gene editing
cell death
disease modeling
Gene Therapy
genetic
inherited disease
retinal degeneration
retinal organoid
stem cell
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Abstract
Language
en
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2213-6711
ISBN
DOI
10.1016/j.stemcr.2020.05.007
PMID
32531192
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